diseases treated with stem cells
Diseases Treated with Stem Cells
Although not all diseases treated with stem cells have been treated specifically with cord blood stem cells, doctors have been using cord blood in lifesaving treatments since 1988. And recently, scientists have discovered some amazing new possibilities for treating diseases and injuries in the future.
Current Stem Cell Applications
Bone Marrow Failure Disorders
Amegakaryocytosis
Aplastic Anemia (Severe)
Blackfan-Diamond Anemia
Congenital Cytopenia*
Congenital Dyserythropoietic Anemia
Dyskeratosis Congenita
Fanconi Anemia
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pure Red Cell Aplasia
Hemoblobinopathies
Beta Thalassemia Major
Sickle Cell Disease
Histiocytic Disorders
Familial Erythrophagocytic Lymphohistiocytosis
Hemophagocytosis
Langerhans' Cell Histiocytosis (Histiocytosis X)
Inherited Immune System Disorders
Chronic Granulomatous Disease
Congenital Neutropenia
Leukocyte Adhesion Deficiency
Severe Combined Immunodeficiencies (SCID) including:
Adenosine Deaminase Deficiency*
Bare Lymphocyte Syndrome
Chediak-Higashi Syndrome*
Kostmann Syndrome
Omenn Syndrome
Purine Nucleoside Phosphorylase Deficiency
Reticular Dysgenesis
Wiskott-Aldrich Syndrome
X-Linked Lymphoproliferative Disorder
Inherited Metabolic Disorders
Adrenoleukodystrophy
Fucosidosis
Gaucher Disease*
Hunter Syndrome (MPS-II)
Hurler Syndrome (MPS-IH)
Krabbe Disease
Lesch-Nyhan Syndrome
Mannosidosis*
Maroteaux-Lamy Syndrome (MPS-VI)
Metachromatic Leukodystrophy
Mucolipidosis II (I-cell Disease)*
Neuronal Ceroid Lipofuscinosis (Batten Disease)*
Niemann-Pick Disease*
Sandhoff Disease*
Sanfilippo Syndrome (MPS-III)
Scheie Syndrome (MPS-IS)
Sly Syndrome
Tay Sachs*
Wolman Disease
Leukemias and Lymphomas
Acute Biphenotypic Leukemia*
Acute Lymphocytic Leukemia (ALL)
Acute Myelogenous Leukemia (AML)
Acute Undifferentiated Leukemia*
Adult T Cell Leukemia/Lymphoma
Chronic Lymphocytic Leukemia (CLL)
Chronic Myelogenous Leukemia (CML)
Hodgkin's Lymphoma
Juvenile Chronic Myelogenous Leukemia (JCML)
Juvenile Myelomonocytic Leukemia (JMML)
Myeloid/Natural Killer (NK) Cell Precursor Acute Leukemia
Non-Hodgkin's Lymphoma
Polymphocytic Leukemia
Myelodysplastic/Myeloproliferative Disorders
Acute Myelofibrosis*
Agnogenic Myeloid Metaplasia (Myelofibrosis)*
Amyloidosis
Chronic Myelomonocytic Leukemia (CMML)
Essential Thrombocythemia*
Polycythemia Vera*
Refractory Anemias (RA) including:
Refractory Anemia with Excess Blasts (RAEB)
Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
Refractory Anemia with Ringed Sideroblasts (RARS)
Plasma Cell Disorders
Multiple Myeloma
Plasma Cell Leukemia
Waldenstrom's Macroglobulinemia
Other Inherited Disorders
Cartilage-Hair Hypoplasia
Congenital Erythropoietic Porphyria (Gunther Disease)
DiGeorge Syndrome
Osteopetrosis
Other Malignancies
Brain Tumors**
Ewing Sarcoma*
Neuroblastoma
Ovarian Cancer**
Renal Cell Carcinoma**
Rhabdomyosarcoma
Small Cell Lung Cancer**
Testicular Cancer**
Thymoma (Thymic Carcinoma)
Other
Chronic Active Epstein Barr
Evans Syndrome
Multiple Sclerosis**
Rhuematoid Arthritis**
Systemic Lupus Erythematosus**
Thymic Dysplasia
*Refer to www.clinicaltrials.gov for additional information
**Not routinely eligible for participation in CBR's Designated Transplant Program Source: Medical literature and www.clinicaltrials.gov